Gene therapy for phenylketonuria (PKU) in China represents a groundbreaking advancement in treating this rare genetic disorder. By delivering a functional PAH gene via viral vectors, this innovative approach aims to restore normal phenylalanine metabolism, reducing reliance on strict diets. Early clinical trials show promising results, with significant drops in phenylalanine levels and improved quality of life. While still in development, this therapy offers hope for a long-term solution. Contact us on WhatsApp +852 6428 1793 to learn more!
Cell and gene therapy for cancer, autoimmune diseases and genetic disorders
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