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GC101 Gene Therapy for Spinal Muscular Atrophy Type 1 – Phase I/II Clinical Trial

Gene Therapy for Spinal Muscular Atrophy Type 1 – Phase I/II Clinical Trial ClinicalTrials.gov Identifier: NCT05824169Sponsor: GeneCradle Inc.Study Title: Safety and Efficacy of GC101 Gene Therapy i...
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