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Advancing Alström Syndrome Treatment in China: Gene Therapy and Clinical Innovations at NCMC, Shanghai

Alström Syndrome (AS) Alström Syndrome (AS) is an ultra-rare genetic disorder characterized by a spectrum of progressive symptoms, including vision and hearing loss, obesity, type 2 diabetes, cardio...
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Advancing Bardet-Biedl Syndrome Treatment in China: Gene Therapy and Clinical Innovations at NCMC, Shanghai

Bardet-Biedl Syndrome (BBS) Bardet-Biedl Syndrome (BBS) is a rare, multisystem genetic disorder characterized by symptoms such as retinal degeneration, obesity, polydactyly, kidney abnormalities, and...
rare-disease-clinical-trials-shanghai

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