Gene Therapy for Spinal Muscular Atrophy Type 1 – Phase I/II Clinical Trial
ClinicalTrials.gov Identifier: NCT05824169Sponsor: GeneCradle Inc.Study Title: Safety and Efficacy of GC101 Gene Therapy i...
aav9-smn1-therapy
GC101 Gene Therapy for Spinal Muscular Atrophy Type 2 – Phase I/II Clinical Trial
ClinicalTrials.gov Identifier: NCT05901987Sponsor: GeneCradle Inc.Study Title: Safety and Efficacy of GC101 Gene The...
aav9-smn1-therapy
Phase III Trial: GC101 Gene Therapy for Type 2 Spinal Muscular Atrophy (SMA)
ClinicalTrials.gov Identifier: NCT06971094Sponsor: GeneCradle Inc.Study Title: Safety and Efficacy Evaluation of GC101 Gen...
aav9-smn1-therapy