What is gene therapy? Gene therapy acts as the lighthouse of contemporary medicine by offering to help correct hereditary afflictions at their very roots—the genome itself. Such treatment involves ...
History and Evolution of Gene Therapy The history and development of gene therapy, a radically new medical intervention that intends to treat or prevent diseases by modifying the genetic material wit...
Genetic disorders and gene therapy Gene therapy has transformed the concept of treatment for a genetic disorder, thus giving hopes to millions across the globe. Therefore, regarding biomedical resear...
FDA approval of gene therapy The FDA has made it possible for people 12 years of age and older who have transfusion-dependent beta-thalassemia (TDT) to use exagamglogene autotemcel (Casgevy, Vertex)....
USFDA approved gene therapy for sickle cell disease The U.S. Food and Drug Administration has granted approval for two significant medications, Casgevy and Lyfgenia, which are the first gene therap...
Gene Therapy Applied to Thalassemia: An Overview Thalassemia is one such blood disorder characterized by the body being unable to produce enough hemoglobin, making life unusually challenging for both...
June 2024: The Food and Drug Administration (FDA) has given accelerated approval to repotrectinib (AUGTYRO, Bristol-Myers Squibb Company) for the treatment of solid tumors in adult and pedia...
May 2024: Imetelstat (Rytelo, Geron Corporation), an oligonucleotide telomerase inhibitor, has been approved by the Food and Drug Administration for use in adults with low- to intermediate-1...
April 2024: The Food and Drug Administration (FDA) granted accelerated approval to tovorafenib (Ojemda, Day One Biopharmaceuticals, Inc.). This approval is specifically for patients aged 6 months and ...
Lutetium Lu 177 dotatate is approved by USFDA for pediatric patients The Food and Drug Administration has approved lutetium Lu 177 dotatate (Lutathera, Advanced Accelerator Applications USA, Inc., a ...