Gene Therapy for Phenylketonuria in China: A Breakthrough Treatment IntroductionPhenylketonuria (PKU) is a rare genetic disorder that affects the body's ability to break down phenylalanine (Phe), an ...
In the constantly shifting field of therapy for cancer, Gamma Delta T Cell therapy presents itself as the new hope treatment. Known primarily for its efficacy in using one's own body's immune system t...
What is gene therapy? Gene therapy acts as the lighthouse of contemporary medicine by offering to help correct hereditary afflictions at their very roots—the genome itself. Such treatment involves ...
History and Evolution of Gene Therapy The history and development of gene therapy, a radically new medical intervention that intends to treat or prevent diseases by modifying the genetic material wit...
FDA approval of gene therapy The FDA has made it possible for people 12 years of age and older who have transfusion-dependent beta-thalassemia (TDT) to use exagamglogene autotemcel (Casgevy, Vertex)....
USFDA approved gene therapy for sickle cell disease The U.S. Food and Drug Administration has granted approval for two significant medications, Casgevy and Lyfgenia, which are the first gene therap...
Gene Therapy Applied to Thalassemia: An Overview Thalassemia is one such blood disorder characterized by the body being unable to produce enough hemoglobin, making life unusually challenging for both...