USFDA approved gene therapy for sickle cell disease The U.S. Food and Drug Administration has granted approval for two significant medications, Casgevy and Lyfgenia, which are the first gene therapies using cell-based technique..
Gene Therapy for Sickle Cell Anemia: An Introduction Gene therapy for sickle cell anemia has been one of the most promising methodologies in the treatment of this genetic disorder. This article takes one deep into the world of ge..
May 2024: Imetelstat (Rytelo, Geron Corporation), an oligonucleotide telomerase inhibitor, has been approved by the Food and Drug Administration for use in adults with low- to intermediate-1 risk myelodysplastic syndrome..
This story is about bone marrow transplant in India. Mukhtar, who is from Assela in Ethiopia, suffers from deadly aplastic anemia. He travels to India for his stem cell transplant. Read the entire story here. Mukhtar Mukhtar is ..