Successful CRISPR Gene Therapies in Practice: Case Studies
Case Studies: Successful CRISPR Gene Therapies in Practice CRISPR, an acronym for Clustered Regularly Interspaced Short Palindromic Repeats, has emerged as a revolutionary instrument in the domain of gene editing, significantly t..
The future of gene therapy: What to expect in the next decade?
Gene therapy Gene therapy, which means changing genes to cure or avert diseases, has progressed significantly in the last number of years. The future of gene therapy looks bright due to inventions in gene editing techniques such ..
CRISPR and gene editing: Revolutionizing gene therapy
Evolution of CRISPR-Cas9 The CRISPR-Cas9 gene-editing tool has changed gene therapy into a means that is more precise, efficient, and versatile when editing genetic code. A technology of this sophistication gives immense scope fo..
Gene therapy in treating cancer: Success stories and challenges
Gene Therapy Gene therapy is such a fast-growing field with enormous potential for the treatment of this disease by targeting genetic mutations that cause it. Gene therapy not only provides new ways of manipulating the genetic ma..
Gene therapy in China
Genetic disorders and gene therapy Gene therapy has transformed the concept of treatment for a genetic disorder, thus giving hopes to millions across the globe. Therefore, regarding biomedical research and infrastructural develop..
First Gene Therapy for Children with Metachromatic Leukodystrophy is Approved by the FDA
FDA approval The U.S. Food and Drug Administration has granted Lenmeldy (atidarsagene autotemcel) approval. The FDA has approved this gene therapy as the first of its kind for the treatment of children with pre-symptomatic late i..
FDA approves gene therapy to treat beta thalassemia
FDA approval of gene therapy The FDA has made it possible for people 12 years of age and older who have transfusion-dependent beta-thalassemia (TDT) to use exagamglogene autotemcel (Casgevy, Vertex). This is a cell therapy that c..
Gene Therapy for Thalassemia
Gene Therapy Applied to Thalassemia: An Overview Thalassemia is one such blood disorder characterized by the body being unable to produce enough hemoglobin, making life unusually challenging for both patients and healthcare provi..
Gene therapy for sickle cell anemia
Gene Therapy for Sickle Cell Anemia: An Introduction Gene therapy for sickle cell anemia has been one of the most promising methodologies in the treatment of this genetic disorder. This article takes one deep into the world of ge..
Mesenchymal stem cell therapy in neurological disorders
Neurological diseases are big problems around the world because they cause a lot of death and disability. Traditional treatments haven't always worked, which has led to a change toward new methods like cell-based therapies. Beca..